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| Filing Date | Reporting Person | Amount Beneficially Owned | % of Class |
|---|---|---|---|
| 2025-02-14 | Sofinnova Partners SAS | 314.26K | 2.60% |
| 2025-02-14 | EcoR1 Capital, LLC | 388.86K | 4.00% |
| 2025-02-14 | Karl Naegler | 314.26K | 2.60% |
| 2025-02-14 | Anta Gkelou | 314.26K | 2.60% |
| 2025-02-14 | Graziano Seghezzi | 314.26K | 2.60% |
| 2025-02-14 | Maina Bhaman | 314.26K | 2.60% |
| 2025-02-14 | Henrijette Richter | 314.26K | 2.60% |
| 2025-02-14 | Antoine Papiernik | 314.26K | 2.60% |
| 2025-02-14 | Sofinnova Capital VI FCPR | 314.26K | 2.60% |
| 2024-07-08 | Westend S.A. | 5.67M | 5.90% |
| 2024-07-08 | Invus Public Equities, L.P. | 5.67M | 5.90% |
| 2024-07-08 | Artal Group S.A. | 5.67M | 5.90% |
| 2024-07-08 | Artal International Management S.A. | 5.67M | 5.90% |
| 2024-07-08 | Artal International S.C.A. | 5.67M | 5.90% |
| 2024-07-08 | Invus Public Equities Advisors, LLC | 5.67M | 5.90% |
| 2024-07-08 | Mr. Amaury Wittouck | 5.67M | 5.90% |
| 2024-07-08 | Stichting Administratiekantoor Westend | 5.67M | 5.90% |
| 2024-06-14 | Felix J. Baker | 9.81M | 9.99% |
| 2024-06-14 | Baker Bros. Advisors LP | 9.81M | 9.99% |
| 2024-06-14 | Baker Bros. Advisors (GP) LLC | 9.81M | 9.99% |
| 2024-06-14 | Julian C. Baker | 9.81M | 9.99% |
| 2024-05-31 | EcoR1 Capital, LLC | 5.72M | 11.00% |
| 2024-05-31 | EcoR1 Capital Fund Qualified, L.P. | 5.39M | 11.00% |
| 2024-05-31 | Oleg Nodelman | 5.72M | 11.00% |
| 2023-06-20 | Knoll Capital Management, LLC | 5.52M | 6.80% |
| 2023-02-14 | Baker Bros. Advisors LP | 3.48M | 6.60% |
| 2023-02-14 | Baker Bros. Advisors (GP) LLC | 3.48M | 6.60% |
| 2023-02-14 | Felix J. Baker | 3.48M | 6.60% |
| 2023-02-14 | Julian C. Baker | 3.48M | 6.60% |
| 2022-04-11 | FMR LLC | 5.68M | 11.00% |
| 2022-04-11 | Abigail P. Johnson | 5.68M | 11.00% |
| 2022-04-08 | EcoR1 Capital, LLC | 5.09M | 11.00% |
| 2022-04-08 | EcoR1 Capital Fund Qualified, L.P. | 4.73M | 11.00% |
| 2022-04-08 | Oleg Nodelman | 5.09M | 11.00% |
| 2022-03-04 | David Kroin | 5.04M | 9.90% |
| 2022-03-04 | Deep Track Capital, LP | 5.04M | 9.90% |
| 2022-03-04 | Deep Track Biotechnology Master Fund, Ltd. | 5.04M | 9.90% |
| 2022-02-14 | Redmile Group, LLC | 2.77M | 9.90% |
| 2022-02-14 | Jeremy C. Green | 2.77M | 9.90% |
| 2022-02-11 | B.V. | 927.0 | 3.10% |
| 2022-02-11 | Coöperatief U.A. | 927.0 | 3.10% |
| 2021-02-16 | Jeremy C. Green | 2.65M | 9.90% |
| 2021-02-16 | Redmile Group, LLC | 2.65M | 9.90% |
| 2021-02-02 | Henrijette Richter (“Richter”) | 3.87M | 13.30% |
| 2021-02-02 | Antoine Papiernik (“Papiernik”) | 3.87M | 13.30% |
| 2021-02-02 | Graziano Seghezzi (“Seghezzi”) | 3.87M | 13.30% |
| 2021-02-02 | Sofinnova Capital VI FCPR (“SC VI”) | 3.87M | 13.30% |
| 2021-02-02 | Sofinnova Partners SAS (“SP SAS”) | 3.87M | 13.30% |
| 2021-02-02 | Denis Lucquin (“Lucquin”) | 3.87M | 13.30% |
| 2021-02-02 | Monique Saulnier (“Saulnier”) | 3.87M | 13.30% |
| 2020-02-11 | Page 3 of 6 Pages | 2.49M | 11.55% |
| 2020-02-11 | Page 2 of 6 Pages | 2.49M | 11.55% |
| 2019-05-03 | Artal Treasury Limited | 535K | 2.50% |
| 2019-05-03 | Mr. Pascal Minne | 1.13M | 5.30% |
| 2019-05-03 | Invus Public Equities, L.P. | 535K | 2.50% |
| 2019-05-03 | Fynveur Management Sàrl | 599.62K | 2.80% |
| 2019-05-03 | Fynveur SCA | 599.62K | 2.80% |
| 2019-05-03 | Artal International S.C.A. | 1.13M | 5.30% |
| 2019-05-03 | Artal Group S.A. | 1.13M | 5.30% |
| 2019-05-03 | Stichting Administratiekantoor Westend | 1.13M | 5.30% |
| 2019-05-03 | Artal International Management S.A. | 1.13M | 5.30% |
| 2019-05-03 | Invus Public Equities Advisors, LLC | 535K | 2.50% |
| 2019-05-03 | Westend S.A. | 1.13M | 5.30% |
| 2019-04-26 | 6.2%(2) | 1.33M | 6.20% |
| 2019-04-26 | in Row (9) | 558.91K | 2.60% |
| 2019-04-26 | 6.2%(1) | 1.33M | 6.20% |
| 2019-04-26 | 6.2%(2) | 1.33M | 6.20% |
| 2019-04-24 | Redmile Group, LLC | 1.89M | 8.80% |
| 2019-04-24 | Jeremy C. Green | 1.89M | 8.80% |
| Date | Stock Price | Shares Outstanding | Market Cap | Cash & Equivalents | Total Debt | Enterprise Value |
|---|---|---|---|---|---|---|
| 2025-12-31 | $0.89 | 12.65M | $11.3M | $37.42M | $135K | -$25.99M |
| 2024-12-31 | $2.01 | 12.54M | $25.2M | $39.68M | $875K | -$13.61M |
| 2023-12-31 | $8.10 | 9.45M | $76.57M | $117.1M | $6.56M | -$33.97M |
| 2022-12-31 | $8.10 | 6.55M | $53.07M | $113.44M | $6.5M | -$53.88M |
| 2021-12-31 | $23.30 | 3.28M | $76.5M | $65.92M | $10.62M | $21.21M |
| 2020-12-31 | $110.90 | 2.6M | $288.77M | $143.18M | $10.77M | $156.36M |
| 2019-12-31 | $122.30 | 1.79M | $218.43M | $113.15M | $11.98M | $117.26M |
| 2018-12-31 | $140.00 | 91437 | $12.8M | $48.58M | $4.39M | -$31.39M |
| 2017-12-31 | $140.00 | 91177 | $12.76M | $61.36M | $3.74M | -$44.86M |
| Date | Stock Price | Shares Outstanding | Market Cap | Cash & Equivalents | Total Debt | Enterprise Value |
|---|---|---|---|---|---|---|
| 2025-06-30 | $1.25 | 12.68M | $15.85M | $34.23M | $546K | -$17.83M |
| 2025-03-31 | $1.08 | 12.54M | $13.55M | $40.28M | $596K | -$26.13M |
| 2024-12-31 | $2.01 | 12.54M | $25.2M | $39.68M | $875K | -$13.61M |
| 2024-09-30 | $4.30 | 12.54M | $53.92M | $59.75M | $2.82M | -$3.01M |
| 2024-06-30 | $6.28 | 12.54M | $78.74M | $77.15M | $4.9M | $6.49M |
| 2024-03-31 | $7.24 | 13.08M | $94.67M | $92.75M | $6.08M | $8M |
| 2023-12-31 | $8.10 | 11.28M | $91.37M | $117.1M | $6.56M | -$19.17M |
| 2023-09-30 | $6.16 | 11.04M | $68M | $107.68M | $3.85M | -$35.82M |
| 2023-06-30 | $8.80 | 8.26M | $72.73M | $135.59M | $4.28M | -$58.58M |
| 2023-03-31 | $7.36 | 7.22M | $53.15M | $110.02M | $5.76M | -$51.11M |
| 2022-12-31 | $8.10 | 7.24M | $58.66M | $113.44M | $6.5M | -$48.28M |
| 2022-09-30 | $13.40 | 7.22M | $96.79M | $99.78M | $6.21M | $3.23M |